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Quality of Life Research

Gepubliceerd in:

30-11-2021

Mapping the Haem-A-QoL to the EQ-5D-5L in patients with hemophilia

Auteurs: Richard Huan Xu, Dong Dong, Nan Luo, Eliza Lai-Yi Wong, Renchi Yang, Junshuai Liu, Huiqin Yuan, Shuyang Zhang

Gepubliceerd in: Quality of Life Research | Uitgave 5/2022

Abstract

Objective

This study’s objective was to develop an algorithm that mapping the Haem-A-QoL scores to EQ-5D-5L utility scores in patients with hemophilia in China.

Methods

A national sample of 862 patients with hemophilia completed both the EQ-5D-5L and Haem-A-QoL instruments. Eight regression models were selected to develop the mapping algorithm, they were: the ordinary least squares, general linear regression, Tobit regression, censored least absolute deviation, mixture beta regression, adjusted limited dependent variable mixture, the two-part, and robust MM-estimator model. Root mean squared error (RMSE), mean absolute error (MAE), and R-square (R²) calculated using the tenfold cross-validation and random sample validation methods were used to assess the predictive ability of the models.

Results

Based on RMSE, MAE, and R², the mixture beta regression model with selected Haem-A-QoL subscale scores as the predicted variables showed the best performance.

Conclusions

Our mapping algorithm bolsters the calculation of QALYs while conducting an economic evaluation of hemophilia-related interventions when only Haem-A-QoL data are available. The external validity of the algorithm should be further assessed in the other populations.

vorige artikel What difference does multiple imputation make in longitudinal modeling of EQ-5D-5L data? Empirical analyses of simulated and observed missing data patterns

volgende artikel The QALY is ableist: on the unethical implications of health states worse than dead

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Titel: Mapping the Haem-A-QoL to the EQ-5D-5L in patients with hemophilia
Auteurs: Richard Huan Xu
Dong Dong
Nan Luo
Eliza Lai-Yi Wong
Renchi Yang
Junshuai Liu
Huiqin Yuan
Shuyang Zhang
Publicatiedatum: 30-11-2021
Uitgeverij: Springer International Publishing
Gepubliceerd in: Quality of Life Research / Uitgave 5/2022
Print ISSN: 0962-9343
Elektronisch ISSN: 1573-2649
DOI: https://doi.org/10.1007/s11136-021-03051-5

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Abstract

Objective

Methods

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Conclusions

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