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Quality of Life Research
Gepubliceerd in: Quality of Life Research 1/2015

01-01-2015 | Quantitative Methods Special Section

Assessment of score- and Rasch-based methods for group comparison of longitudinal patient-reported outcomes with intermittent missing data (informative and non-informative)

Auteurs: Élodie de Bock, Jean-Benoit Hardouin, Myriam Blanchin, Tanguy Le Neel, Gildas Kubis, Véronique Sébille

Gepubliceerd in: Quality of Life Research | Uitgave 1/2015

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Abstract

Purpose

The purpose of this study was to identify the most adequate strategy for group comparison of longitudinal patient-reported outcomes in the presence of possibly informative intermittent missing data. Models coming from classical test theory (CTT) and item response theory (IRT) were compared.

Methods

Two groups of patients’ responses to dichotomous items with three times of assessment were simulated. Different cases were considered: presence or absence of a group effect and/or a time effect, a total of 100 or 200 patients, 4 or 7 items and two different values for the correlation coefficient of the latent trait between two consecutive times (0.4 or 0.9). Cases including informative and non-informative intermittent missing data were compared at different rates (15, 30 %). These simulated data were analyzed with CTT using score and mixed model (SM) and with IRT using longitudinal Rasch mixed model (LRM). The type I error, the power and the bias of the group effect estimations were compared between the two methods.

Results

This study showed that LRM performs better than SM. When the rate of missing data rose to 30 %, estimations were biased with SM mainly for informative missing data. Otherwise, LRM and SM methods were comparable concerning biases. However, regardless of the rate of intermittent missing data, power of LRM was higher compared to power of SM.

Conclusions

In conclusion, LRM should be favored when the rate of missing data is higher than 15 %. For other cases, SM and LRM provide similar results.
vorige artikel Time to health-related quality of life score deterioration as a modality of longitudinal analysis for health-related quality of life studies in oncology: do we need RECIST for quality of life to achieve standardization?
volgende artikel Joint models for predicting transplant-related mortality from quality of life data
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Metagegevens
Titel
Assessment of score- and Rasch-based methods for group comparison of longitudinal patient-reported outcomes with intermittent missing data (informative and non-informative)
Auteurs
Élodie de Bock
Jean-Benoit Hardouin
Myriam Blanchin
Tanguy Le Neel
Gildas Kubis
Véronique Sébille
Publicatiedatum
01-01-2015
Uitgeverij
Springer International Publishing
Gepubliceerd in
Quality of Life Research / Uitgave 1/2015
Print ISSN: 0962-9343
Elektronisch ISSN: 1573-2649
DOI
https://doi.org/10.1007/s11136-014-0648-1

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