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Quality of Life Research

Gepubliceerd in:

17-06-2022

Application of validated mapping algorithms between generic PedsQL scores and utility values to individuals with sickle cell disease

Auteurs: Boshen Jiao, Jane S. Hankins, Beth Devine, Martha Barton, M. Bender, Anirban Basu

Gepubliceerd in: Quality of Life Research | Uitgave 9/2022

Abstract

Purpose

There is a paucity of empirically estimated health state utility (HSU) values to estimate health-related quality of life among individuals with sickle cell disease (SCD). This study aims to map the Pediatric Quality of Life Inventory generic core scales (PedsQL GCS) to HSUs for children and adolescents with SCD in the United States, using published algorithms, and to assess the construct validity of these HSUs against SCD-specific PedsQL scores.

Methods

We used the published mapping algorithms identified in four published articles, in which the PedsQL GCS was mapped to either the EuroQol-5 Dimension 3-Level, Youth Version or the Child Health Utility 9-Dimension to obtain HSUs. We employed the algorithms to calculate HSUs for a sample of children and adolescents from the Sickle Cell Clinical Research and Intervention Program. To assess the construct validity of the mapped HSUs in SCD patients, we computed Spearman’s correlation coefficient comparing the HSUs with the PedsQL SCD total score and separately with each PedsQL SCD dimension-specific score.

Results

The mean mapped HSU across published algorithms was 0.792 (95% CI: 0.782–0.801). It was significantly higher among children aged 5–12 years than children aged 13–17 years. The Spearman’s correlation coefficient for HSUs versus PedsQL SCD total scores was 0.64 (95% CI: 0.57–0.71). Correlations ranged from 0.40 (95% CI: 0.32–0.48) to 0.60 (95% CI: 0.54–0.66) for HSUs versus PedsQL SCD dimension-specific scores.

Conclusions

The existing mapping algorithms show acceptable construct validity in children and adolescents with SCD. Additional algorithms are needed for adults and for specific SCD comorbidities.

vorige artikel Identifying health-related quality of life cut-off scores that indicate the need for supportive care in young adults with cancer

volgende artikel The use of composite time trade-off and discrete choice experiment methods for the valuation of the Short Warwick-Edinburgh Mental Well-being Scale (SWEMWBS): a think-aloud study

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Titel: Application of validated mapping algorithms between generic PedsQL scores and utility values to individuals with sickle cell disease
Auteurs: Boshen Jiao
Jane S. Hankins
Beth Devine
Martha Barton
M. Bender
Anirban Basu
Publicatiedatum: 17-06-2022
Uitgeverij: Springer International Publishing
Gepubliceerd in: Quality of Life Research / Uitgave 9/2022
Print ISSN: 0962-9343
Elektronisch ISSN: 1573-2649
DOI: https://doi.org/10.1007/s11136-022-03167-2

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Abstract

Purpose

Methods

Results

Conclusions

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